- Title
- Combined enzyme replacement and haematopoietic stem cell transplantation in Hurler syndrome
- Creator
- Bijarnia, Sunita; Shaw, Peter; Vimpani, Anne; Smith, Robert; Pacey, Verity; O'Grady, Helen; Christodoulou, John; Sillence, David
- Relation
- Journal of Paediatrics and Child Health Vol. 45, Issue 7-8, p. 469-472
- Publisher Link
- http://dx.doi.org/10.1111/j.1440-1754.2009.01537.x
- Publisher
- Wiley-Blackwell Publishing
- Resource Type
- journal article
- Date
- 2009
- Description
- We report the long-term follow-up of successful treatment of mucopolysaccharidosis type I H (MPS IH, Hurler syndrome) with combined enzyme replacement therapy and haematopoietic progenitor stem cell transplant.
- Subject
- enzyme replacement therapy; haematopoietic stem cell transplantation; Hurler syndrome; laronidase
- Identifier
- uon:7086
- Identifier
- http://hdl.handle.net/1959.13/925069
- Identifier
- ISSN:1034-4810
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